This news article, written by 4-traders and the pharma letters, describes the path that led to the agreement between Chugai, who discovered CNP, and BioMarin.

Researchers are failing to submit their clinical trials' results in clinicaltrials.gov.

This study not only means to understand the natural history of achondroplasia (what complications occur, how often, average life span, etc.), but also aims to build a global patient registry. What is the purpose of a patient registry? Know more about it here.

What are the next steps for BMN-111? Here you can find a timetable for what is planned for this rdug in development.

New treatments using the CRISPR/Cas9 gene editing tool are being developed. In order to understand how these would work here is a short vídeo and article about this possible excision of the mutation and substitution with the non-mutated gene.

CRISPR/Cas9 is powerful new gene editing tool, making development of new treatments easier, faster and cheaper. It's potential for use in humans is currently under study, but how does it work exactly, and why is it so versatile? Learn more about this revolutionary technology here.