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Survey about achondroplasia
We have designed a questionnaire with the purpose to better know the population connected to achondroplasia.
The questionnaire is optional and anonymous. The data obtained will be used for statistical purposes and to better understand the natural history of achondroplasia. Please consider answering.
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BioMarin investors page announces

2015-11-25Research
BioMarin intends to move into Phase 3 study discussions on the next stage of development with health authorities with a dose of 15 micrograms per kilogram daily. Also, a new cohort, designed to test a new dose regimen has completed enrollment for the Phase 2 study.

New cohort revealed for phase 2 of BMN-111

2015-10-19Research
A new cohort for the phase 2 clinical trial for BMN-111 has been revealed, learn more about it here.

BMN-111 phase 2 results presented at the ASBMR 2015 meeting

2015-10-15Research
Recap on the results from the first 6 months of the phase 2 clinical trial for BMN-111, elicited by a presentation at the American Society for Bone and Mineral Research of 2015.

Soluble FGFR3 going forward with Therachon

2015-10-01Research
Soluble FGFR3, a drug for achondroplasia under development by TherAchon is moving towards clinical trials. See the summary of their press release here.

B-701 - New potential treatment for achondroplasia

2015-08-25Research
New potential treatment for achondroplasia being developed by BioClin Therapeutics. It's based on monoclonal antibodies and is also being tested for Urothelial Cell Carcinoma.

Statins for achondroplasia, at the 12th ISDS meeting - part 1

2015-08-09Research
This is a summary of Dr. Tsumaki's lecture at the 12th ISDS meeting about statins as a potential treatment for achondroplasia.
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