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Survey about achondroplasia
We have designed a questionnaire with the purpose to better know the population connected to achondroplasia.
The questionnaire is optional and anonymous. The data obtained will be used for statistical purposes and to better understand the natural history of achondroplasia. Please consider answering.
If you would like to take the survey later, you can click on the link at the top "Register at BA"

BMN-111 Phase 2: study 111-202 and extension study 111-205

2016-05-13Research
There are two studies by BioMarin in Phase 2 clinical trials where BMN-111 (vosoritide) is being administered. They have different objectives and durations, which can be consulted here.

Update in multicenter study from BioMarin

2016-04-21Research
Biomarin is sponsoring and coordinating a study for the study of growth patterns of Achondroplasia in children and adolescents in several centers in Europe and North America. Find out where it's being conduced here.

Vosoritide for Achondroplasia - Research and Development day 20th April 2016

2016-04-21Research
On Research and Development Day BioMarin presented updates for Vosoritide (BMN-111) clinical trials. See the summary of these updates here.

ReAch Achondroplasia Registry

2016-04-11Research
Prof. Krejcis team is researching FGF signaling mechanisms, in particular, pathological FGFRs, such as FGFR3, which causes achondroplasia. His team also manages ReACH, standing for Registry of Achondroplasia, which means to serve as a tool for clinicians and healthcare providers to conduct research.

Patent and license agreement for CNP

2016-03-28Research
This news article, written by 4-traders and the pharma letters, describes the path that led to the agreement between Chugai, who discovered CNP, and BioMarin.

Science with no results shared

2016-03-04Research
Researchers are failing to submit their clinical trials' results in clinicaltrials.gov.
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