Beyond Achondroplasia

Growing together with Clara

July 14, 2014
by inesp.alves
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One importante step forward on rare diseases registry

From now on, all sponsors of clinical trials have to share and publish relevant information about the trial on the EudraCT , the European Clinical Trials Database. Trials results information will be publicly available at the EU Clinical Trials Register including summary results from … Continue reading

Rare diseases and orphan drugs market

July 11, 2014 by inesp.alves | 0 comments

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May 7, 2013
by inesp.alves
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EMA granted BMN-111 an orphan designation

The ceiling for orphan designation is 5 people affected in 10.000. Achondroplasia in the European Union affects in 2013, 0,42 people in 10.000, existing 21.000 people with achondroplasia in EU (we are 509 million people in EU). EMA, the European … Continue reading

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